Chinese Researchers Notch Major Milestone in Developing Gene Editing System Against Autism
Chinese researchers may have scored a major win in the fight against autism after they successfully edited a mutated gene associated with autism in mice. The research team developed a genome-editing system capable of treating ASD-related mutations in mice using base editing in the brain. This treatment represents the first-ever injection with the ability to reverse autism symptoms, at least in mouse models, and could open the door to the development of alternative treatments for other neurodevelopmental disorders. The injection corrects mutations in the MEF2C gene, which typically occur in patients with autism spectrum disorder (ASD). Estimates from the United…











